Overview

Definition: Idiopathic Thrombocytopenic Purpura (ITP) is an autoimmune disorder characterized by isolated thrombocytopenia (low platelet count) in the absence of other identifiable causes, leading to increased risk of bleeding.
Epidemiology:
-It is the most common acquired bleeding disorder in children
-Acute ITP typically affects children aged 2-10 years, with a slight male predominance
-Incidence is estimated at 1-3 per 100,000 children per year
-Chronic ITP is less common in childhood and more prevalent in adults.
Clinical Significance:
-ITP is significant due to the potential for severe bleeding, especially intracranial hemorrhage, though rare
-Understanding management strategies is crucial for preventing complications and distinguishing it from other causes of thrombocytopenia, a common scenario in pediatric emergency and outpatient settings relevant for DNB and NEET SS exams.

Clinical Presentation

Symptoms:
-Often asymptomatic with incidental finding of low platelets
-Easy bruising (purpura)
-Petechiae, especially on dependent areas or pressure points
-Bleeding from gums or nose (epistaxis)
-Hematuria or menorrhagia in older girls
-Rarely, signs of internal hemorrhage such as abdominal pain or neurological symptoms.
Signs:
-Isolated thrombocytopenia (<100,000/µL) on complete blood count
-Normal or slightly enlarged spleen
-Absence of fever or signs of infection (unless concurrent)
-Examination for other signs of bleeding (e.g., conjunctival petechiae, hematoma formation)
-Absence of hepatosplenomegaly or lymphadenopathy, which would suggest other causes.
Diagnostic Criteria:
-Diagnosis is primarily clinical and laboratory-based
-Key criteria include: isolated thrombocytopenia
-absence of splenomegaly (usually)
-normal white blood cell and red blood cell counts
-absence of other causes of thrombocytopenia (e.g., leukemia, sepsis, drug-induced thrombocytopenia, inherited disorders)
-Platelet count < 150,000/µL with documentation of the diagnosis and exclusion of other causes.

Diagnostic Approach

History Taking:
-Detailed history of bleeding onset and duration
-Recent viral illness or vaccination (within 2-4 weeks) preceding acute ITP
-Family history of bleeding disorders
-Medication history (e.g., aspirin, NSAIDs, certain antibiotics)
-Inquiry about symptoms suggestive of systemic illness or malignancy
-Assess for any signs of recent trauma.
Physical Examination:
-Thorough skin examination for petechiae, purpura, ecchymoses
-Palpate abdomen for splenomegaly
-Examine for mucosal bleeding (oral, nasal)
-Assess for any signs of neurological deficit
-Evaluate lymph nodes for enlargement
-Look for signs of sepsis or systemic infection.
Investigations:
-Complete blood count (CBC) with differential and platelet count is essential, showing isolated thrombocytopenia
-Peripheral blood smear examination is critical to rule out pseudothrombocytopenia and assess platelet morphology, looking for normal-sized platelets
-Coagulation profile (PT, aPTT) should be normal
-Bone marrow aspiration and biopsy is generally not indicated in typical cases of acute ITP in children but may be considered in refractory cases, atypical presentations, or if a secondary cause is suspected
-Serological tests for infections like HIV, HCV, H
-pylori are generally not recommended in routine childhood acute ITP.
Differential Diagnosis:
-Other causes of thrombocytopenia: Acute leukemia (look for abnormal blast cells, pancytopenia)
-Sepsis (look for fever, signs of infection, coagulopathy)
-Viral infections (e.g., EBV, CMV causing secondary thrombocytopenia)
-Drug-induced thrombocytopenia
-Inherited platelet disorders
-Systemic lupus erythematosus (SLE) or other autoimmune disorders
-Hemolytic Uremic Syndrome (HUS) (look for anemia, renal dysfunction, schistocytes)
-Pseudothrombocytopenia (platelet satellitism on EDTA tube)
-Congenital amegakaryocytic thrombocytopenia.

Management

Initial Management:
-For mild to moderate ITP (platelet count > 20,000-30,000/µL with no significant bleeding), observation may be the initial approach
-Avoid trauma and contact sports
-Educate parents on signs of bleeding requiring immediate medical attention.
Medical Management:
-Treatment is indicated for symptomatic bleeding or very low platelet counts (<10,000-20,000/µL)
-Options include: Intravenous Immunoglobulin (IVIG) 1 g/kg/day for 1-2 days or 0.8 g/kg/day for 2 days
-Corticosteroids (e.g., Prednisolone 1-2 mg/kg/day orally or Dexamethasone pulses)
-These treatments aim to rapidly increase platelet count by reducing platelet destruction or increasing production
-Rituximab is an option for refractory chronic ITP
-Thrombopoietin receptor agonists (e.g., Eltrombopag) are generally reserved for chronic refractory ITP in older children or adults.
Surgical Management:
-Splenectomy is rarely indicated in childhood ITP and is reserved for cases of chronic refractory ITP that have failed multiple medical therapies, usually after puberty
-It is not a first-line treatment.
Supportive Care:
-Close monitoring of platelet counts and signs of bleeding
-Parental education on disease course and management
-Strict avoidance of NSAIDs and aspirin due to their antiplatelet effects
-Prompt attention to any significant bleeding episodes
-Counseling on activity restrictions.

Observation Vs Treatment Strategy

Observation Strategy:
-Observation is suitable for asymptomatic children with platelet counts > 20,000-30,000/µL
-In most cases of acute childhood ITP, spontaneous remission occurs within weeks to months
-This approach minimizes exposure to side effects of medications.
Treatment Indications:
-Treatment is generally recommended for children with platelet counts < 10,000-20,000/µL, or any child with bleeding (mucosal bleeding, petechiae beyond a few mm, purpura, ecchymoses)
-Severe bleeding (e.g., gastrointestinal, genitourinary, intracranial) requires urgent intervention regardless of platelet count.
Ivig Role:
-IVIG is effective in rapidly increasing platelet counts, making it useful for managing acute, significant bleeding or to achieve a higher platelet count for procedures
-Its effect is transient, typically lasting a few weeks
-Dose: 1 g/kg/day for 1-2 days or 0.8 g/kg/day for 2 days.
Steroid Role:
-Corticosteroids, such as oral prednisolone (1-2 mg/kg/day), are also effective in increasing platelet counts and are often used as a first-line treatment for symptomatic ITP
-They can induce longer remissions compared to IVIG but have more systemic side effects with prolonged use
-Dexamethasone pulse therapy (e.g., 0.6 mg/kg/day for 4 days) is also an option.

Complications

Early Complications:
-Severe bleeding (e.g., intracranial hemorrhage, gastrointestinal bleeding, prolonged epistaxis)
-Anemia due to blood loss
-Side effects from medications (e.g., allergic reactions to IVIG, hyperglycemia, mood changes, increased infection risk with steroids).
Late Complications:
-Development of chronic ITP (>12 months duration), which is less common in children than acute ITP
-Psychological impact on child and family
-Long-term effects of steroid therapy if used repeatedly or for extended periods (e.g., growth retardation, Cushingoid features).
Prevention Strategies:
-Careful monitoring for bleeding
-Prompt initiation of treatment when indicated
-Patient and family education on avoiding trauma and recognizing bleeding symptoms
-Judicious use of medications and monitoring for their side effects
-Avoiding unnecessary invasive procedures in patients with severe thrombocytopenia.

Prognosis

Factors Affecting Prognosis:
-Most children (about 80%) with acute ITP achieve spontaneous remission within 6 months
-Factors associated with chronic ITP include older age at diagnosis, very low initial platelet counts, and presence of specific autoantibodies
-Severity of initial bleeding can be a factor.
Outcomes:
-The prognosis for acute childhood ITP is generally excellent, with the vast majority recovering fully
-Chronic ITP, while less common, can require long-term management and may impact quality of life.
Follow Up:
-Children with acute ITP who recover generally do not require long-term follow-up once platelet counts normalize and bleeding resolves
-Those who develop chronic ITP require regular monitoring by a pediatric hematologist, including platelet counts and assessment for bleeding and medication-related side effects.

Key Points

Exam Focus:
-DNB/NEET SS frequently test the distinction between acute and chronic ITP in children, indications for treatment (bleeding vs
-platelet count), first-line agents (IVIG/Steroids), and distinguishing ITP from other causes of thrombocytopenia
-Remember that bone marrow biopsy is NOT routinely needed in children with typical ITP presentation.
Clinical Pearls:
-Always consider concurrent viral illness or recent vaccination in the history of acute ITP
-A peripheral blood smear is crucial to rule out pseudothrombocytopenia and assess platelet size
-Observe asymptomatic children with platelet counts >20-30k/µL
-Treat symptomatic children or those with counts <10-20k/µL
-IVIG offers rapid but transient platelet elevation
-steroids offer sustained increase but with more side effects.
Common Mistakes:
-Over-treating asymptomatic children with low platelet counts
-Failing to consider other causes of thrombocytopenia in atypical presentations (e.g., child with fever and petechiae and abnormal WBC)
-Delaying treatment in children with significant bleeding
-Relying solely on platelet count without assessing bleeding status for treatment decisions
-Ordering unnecessary investigations like bone marrow aspiration in routine acute ITP.